This activity will provide an interactive, patient-focused learning experience on the multidisciplinary management of patients with Fabry disease, a rare multisystemic lysosomal storage disorder resulting from α-galactosidase A (α-Gal A) deficiency leading to progressive accumulation of globotriaosylceramide (Gb3) in diverse tissues and organs, including the heart and kidneys. During this engaging webcast you will hear patients’ personal experiences and be involved in clinical challenges to test your knowledge. The clinical journey from diagnosis to treatment will be analyzed, and best practices for multidisciplinary management will be discussed. Additionally, the experts will review the latest clinical evidence on novel therapies and provide their perspectives on treatment strategies.
This activity is supported by an independent educational grant from Amicus Therapeutics Inc.